gene therapy
Published research on gene therapy.

A 2026 twitcher-mouse study found that adenine base editing corrected only about 0.5% of genomic DNA and 5% of mRNA in a Krabbe disease model, yet that low editing signal restored GALC enzym…
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A 2026 Nature Communications study found that Mecp2 overexpression deregulated approximately 5,000 genes in mouse neural progenitor cells but only approximately 500 mostly small-change genes…
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Parkinson’s disease (PD), a degenerative disorder that predominantly affects the motor system, has long been a challenging condition to manage due to its complex pathology and the limited ef…
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Epilepsy affects over 50 million people worldwide, making it one of the most common neurological disorders globally. For many living with epilepsy, achieving reliable seizure control remains…
Read article →Despite the fact that pharmaceutical companies continue to promote the concept of “chemical imbalances” as the root cause of depression, this is a vast oversimplification of an infinitely mo…
Read article →When it comes to depression, most people are looking for a treatment that allows them to feel happier, while minimizing potential side effects. There are many antidepressants on the market, …
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